Mucopolysaccharidosis IIIB Completed Phase 1 / 2 Trials for Lesinidase alfa (DB15267)

Also known as: MPS 3 B / MPS IIIB (Sanfilippo Syndrome) / Sanfilippo B / Mucopolysaccharidosis III-B / Sanfilippo Syndrome B / Mucopolysaccharidosis Type 3 B / Sanfilippo Syndrome Type B / MPS III B / Mucopolysaccharidosis III, Type B (MPS IIIB) / Mucopolysaccharidosis Type IIIB / MPS IIIB (Sanfilippo B Syndrome) / Sanfilippo mucopolysaccharidoses / Mucopolysaccharidosis, MPS-III-B (disorder)

IndicationStatusPhase
DBCOND0074556 (Mucopolysaccharidosis IIIB)Completed1 / 2
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT02324049
Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 in Mucopolysaccharidosis III, Type B (MPS IIIB)Treatment