Mucopolysaccharidosis IIIB Terminated Phase 1 / 2 Trials for Lesinidase alfa (DB15267)
Also known as: MPS 3 B / MPS IIIB (Sanfilippo Syndrome) / Sanfilippo B / Mucopolysaccharidosis III-B / Sanfilippo Syndrome B / Mucopolysaccharidosis Type 3 B / Sanfilippo Syndrome Type B / MPS III B / Mucopolysaccharidosis III, Type B (MPS IIIB) / Mucopolysaccharidosis Type IIIB / MPS IIIB (Sanfilippo B Syndrome) / Sanfilippo mucopolysaccharidoses / Mucopolysaccharidosis, MPS-III-B (disorder)
| Indication | Status | Phase |
|---|---|---|
| DBCOND0074556 (Mucopolysaccharidosis IIIB) | Terminated | 1 / 2 |
| clinicaltrials.gov Identifier | Title | Purpose | Drugs |
|---|---|---|---|
| NCT02618512 | A Open Label Study in Previously Studied, SBC-103 Treatment Naïve MPS IIIB Subjects to Investigate the Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 Administered Intravenously | Treatment |