Mucopolysaccharidosis IIIB Enrolling by Invitation Phase 4 Trials for Tralesinidase alfa (DB17657)

Back to Mucopolysaccharidosis IIIB

Also known as: MPS 3 B / MPS IIIB (Sanfilippo Syndrome) / Sanfilippo B / Mucopolysaccharidosis III-B / Sanfilippo Syndrome B / Mucopolysaccharidosis Type 3 B / Sanfilippo Syndrome Type B / MPS III B / Mucopolysaccharidosis III, Type B (MPS IIIB) / Mucopolysaccharidosis Type IIIB / MPS IIIB (Sanfilippo B Syndrome) / Sanfilippo mucopolysaccharidoses / Mucopolysaccharidosis, MPS-III-B (disorder)

IndicationStatusPhase
DBCOND0074556 (Mucopolysaccharidosis IIIB)Enrolling by Invitation4
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT05492799
Safety, Tolerability and Efficacy of ICV AX 250 Treatment in MPS IIIB -OLETreatment