Mucopolysaccharidosis IV Type A

Also known as: MPS IVA / Mucopolysaccharidosis Type IVA / Morquio A Disease / Morquio A Syndrome / Morquio Syndrome A / Mucopolysaccharidosis IVA / Mucopolysaccharidosis IVA (Morquio A Syndrome) / Morquio A mucopolysaccharidoses / Mucopolysaccharidosis, MPS-IV-A (disorder) / Deficiency of N-acetylgalactosamine-6-sulfatase (finding) / Mucopolysaccharidosis Type IV A

DrugDrug NameDrug Description
DB09051Elosulfase alfaA lysosomal glycosaminoglycan (GAG)-specific enzyme indicated as an enzyme replacement therapy for Mucopolysaccharidosis type IV A.
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB01272Alglucosidase alfa1Recruiting1
DB09051Elosulfase alfa1Recruiting1
DB01279Galsulfase1Recruiting1
DB01271Idursulfase1Recruiting1
DB00090Laronidase1Recruiting1
DB11563Sebelipase alfa1Recruiting1
DB12366Vestronidase alfa1Recruiting1
DB09051Elosulfase alfa1 / 2Completed1
DB09051Elosulfase alfa1 / 2Terminated1
DB11928Vosoritide1 / 2Recruiting1
DB09051Elosulfase alfa2Completed1
DB09051Elosulfase alfa2Terminated2
DB11735Galactose2Completed1
DB11735Galactose2Terminated2
DB00678Losartan2Active Not Recruiting1
DB09051Elosulfase alfa3Completed3
DB11735Galactose3Completed1
DB09051Elosulfase alfaNot AvailableApproved for Marketing1
DB09051Elosulfase alfaNot AvailableCompleted1
DB09051Elosulfase alfaNot AvailableRecruiting1