Propionic Acidemia, Type I and/or Type II

Also known as: Propionic acidaemia / Propionic acidemia / Ketotic glycinaemia / Ketotic glycinemia / Propionic acidemia (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB06775Carglumic acid2Completed1