Propionic Acidemia, Type I and/or Type II
Also known as: Propionic acidaemia / Propionic acidemia / Ketotic glycinaemia / Ketotic glycinemia / Propionic acidemia (disorder)
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
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DB06775 | Carglumic acid | 2 | Completed | 1 |