Late Onset Pompe Disease
Also known as: Late-onset Pompe Disease / Pompe Disease Late-Onset / Pompe Disease (Late-Onset)
Drug | Drug Name | Drug Description |
---|---|---|
DB16099 | Avalglucosidase alfa | A lysosomal glycogen-specific enzyme that is used to treat patients one year of age and older with late-onset Pompe disease, or lysosomal acid alpha-glucosidase (GAA) deficiency. |
DB16708 | Cipaglucosidase alfa | A recombinant human acid alpha-glucosidase used to treat late-onset Pompe disease in adults. |
Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB01272 | Alglucosidase alfa | 2 | Completed | 2 |
DB01407 | Clenbuterol | 2 | Withdrawn | 1 |
DB01272 | Alglucosidase alfa | 3 | Completed | 3 |
DB16708 | Cipaglucosidase alfa | 3 | Active Not Recruiting | 1 |
DB16708 | Cipaglucosidase alfa | 3 | Completed | 1 |
DB16708 | Cipaglucosidase alfa | 3 | Recruiting | 1 |
DB00419 | Miglustat | 3 | Active Not Recruiting | 1 |
DB00419 | Miglustat | 3 | Completed | 1 |
DB00419 | Miglustat | 3 | Recruiting | 1 |
DB17665 | Reveglucosidase alfa | 3 | Terminated | 1 |
DB01272 | Alglucosidase alfa | 4 | Completed | 2 |
DB01272 | Alglucosidase alfa | Not Available | Approved for Marketing | 1 |
DB01272 | Alglucosidase alfa | Not Available | Unknown Status | 1 |