Acute Hepatic Porphyria (AHP)

Also known as: Acute Hepatic Porphyria / ALAD porphyria / Porphobilinogen synthase deficiency (disorder) / Porphyria acute / Porphyria, Acute Intermittent / Acute intermittent porphyria / Acute intermittent porphyria (disorder)

DrugDrug NameDrug Description
DB15066GivosiranA 5-aminolevulinic acid synthase-directed small interfering RNA (siRNA) used in the prophylaxis of acute hepatic porphyria.
DB13387HematinNot Annotated
DrugDrug NameTargetType
DB15066GivosiranALAS1 mRNAtarget
DrugDrug NamePhaseStatusCount
DB15066Givosiran1Completed1
DB15066Givosiran3Completed1
DB15066GivosiranNot AvailableNo Longer Available1