Acute Hepatic Porphyria (AHP)
Also known as: Acute Hepatic Porphyria / ALAD porphyria / Porphobilinogen synthase deficiency (disorder) / Porphyria acute / Porphyria, Acute Intermittent / Acute intermittent porphyria / Acute intermittent porphyria (disorder)
Drug | Drug Name | Drug Description |
---|---|---|
DB15066 | Givosiran | A 5-aminolevulinic acid synthase-directed small interfering RNA (siRNA) used in the prophylaxis of acute hepatic porphyria. |
DB13387 | Hematin | Not Annotated |
Drug | Drug Name | Target | Type |
---|---|---|---|
DB15066 | Givosiran | ALAS1 mRNA | target |