Classic Galactosemia

Also known as: Deficiency of uridine triphosphate-hexose-1-phosphate uridylyltransferase (disorder) / Deficiency of UDPglucose-hexose-1-phosphate uridylyltransferase (disorder) / Galactose-1-Phosphate Uridyl-Transferase Deficiency Disease

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB16707Gavorestat1 / 2Completed1
DB15993Arginine aspartate2Completed1
DB16707Gavorestat2 / 3Active Not Recruiting1
DB16707Gavorestat3Active Not Recruiting1