Gaucher Disease, Type II Active Not Recruiting Phase 1 / 2 Trials for Methylprednisolone (DB00959)
Also known as: Type II Gaucher Disease / Gaucher's disease type II / Gaucher Disease, Type 2 / Type 2 Gaucher Disease / Acute neuronopathic Gaucher's disease (disorder)
| Indication | Status | Phase |
|---|---|---|
| DBCOND0117120 (Gaucher Disease, Type II) | Active Not Recruiting | 1 / 2 |
| clinicaltrials.gov Identifier | Title | Purpose | Drugs |
|---|---|---|---|
| NCT04411654 | Phase 1/2 Clinical Trial of PR001 in Infants With Type 2 Gaucher Disease (PROVIDE) | Treatment |