PAH Deficiency

Also known as: Classical phenylketonuria / Classical phenylketonuria (disorder) / Phenylketonuria I / Phenylpyruvic oligophrenia

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB17684HMI-1031Terminated1
DB00360Sapropterin4Unknown Status1