Polyneuropathies caused by Hereditary transthyretin-mediated amyloidosis

DrugDrug NameDrug Description
DB16199EplontersenA transthyretin antisense oligonucleotide used to treat polyneuropathy of hereditary transthyretin-mediated amyloidosis.
DB14713InotersenAn antisense oligonucleotide used to treat polyneuropathy of hereditary transthyretin-mediated amyloidosis.
DrugDrug NamePhaseStatusCount