Acid Sphingomyelinase Deficiency (ASMD)
Also known as: Human Acid Sphingomyelinase Deficiency / Acid Sphingomyelinase Deficiency / Acid Sphingomyelinase-deficient Niemann-Pick Disease / Niemann-Pick disease, unspecified / Niemann-Pick disease / Sphingomyelin/cholesterol lipidosis (disorder) / Sphingomyelin lipidosis / Niemann-Pick Diseases
| Drug | Drug Name | Drug Description |
|---|---|---|
| DB12835 | Olipudase alfa | A recombinant human acid sphingomyelinase used to treat Acid Sphingomyelinase Deficiency (ASMD) in children and adults. |
| Drug | Drug Name | Target | Type |
|---|
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB12835 | Olipudase alfa | 1 | Completed | 1 |
| DB12835 | Olipudase alfa | Not Available | Recruiting | 2 |