Acid Sphingomyelinase Deficiency (ASMD)

Also known as: Human Acid Sphingomyelinase Deficiency / Acid Sphingomyelinase Deficiency / Acid sphingomyelinase deficiency (ASMD) NOS / Sphingomyelin/cholesterol lipidosis (disorder) / Niemann-Pick disease / Sphingomyelin lipidosis / Niemann-Pick Diseases

DrugDrug NameDrug Description
DB12835Olipudase alfaA recombinant human acid sphingomyelinase used to treat Acid Sphingomyelinase Deficiency (ASMD) in children and adults.
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB12835Olipudase alfa1Completed1
DB12835Olipudase alfaNot AvailableRecruiting1