Acid Sphingomyelinase Deficiency (ASMD) Completed Phase 1 Trials for Olipudase alfa (DB12835)

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Also known as: Human Acid Sphingomyelinase Deficiency / Acid Sphingomyelinase Deficiency / Acid sphingomyelinase deficiency (ASMD) NOS / Sphingomyelin/cholesterol lipidosis (disorder) / Niemann-Pick disease / Sphingomyelin lipidosis / Niemann-Pick Diseases

Indication	Status	Phase
DBCOND0147964 (Acid Sphingomyelinase Deficiency (ASMD))	Completed	1

clinicaltrials.gov Identifier	Title	Purpose	Drugs
NCT01722526	Tolerability and Safety Study of Recombinant Human Acid Sphingomyelinase in Acid Sphingomyelinase Deficiency Patients	Treatment	Olipudase alfa (DB12835)