Acid Sphingomyelinase Deficiency (ASMD) Recruiting Phase Trials for Olipudase alfa (DB12835)
Also known as: Human Acid Sphingomyelinase Deficiency / Acid Sphingomyelinase Deficiency / Acid sphingomyelinase deficiency (ASMD) NOS / Sphingomyelin/cholesterol lipidosis (disorder) / Niemann-Pick disease / Sphingomyelin lipidosis / Niemann-Pick Diseases
| Indication | Status | Phase |
|---|---|---|
| DBCOND0147964 (Acid Sphingomyelinase Deficiency (ASMD)) | Recruiting | Not Available |
| clinicaltrials.gov Identifier | Title | Purpose | Drugs |
|---|---|---|---|
| NCT05359276 | Data Analysis of Adult and Pediatric Participants With Acid Sphingomyelinase Deficiency (ASMD) on Early Access to Olipudase Alfa in France |