Nusinersen sodiumProduct ingredient for Nusinersen

Name
Nusinersen sodium
Drug Entry
Nusinersen

An antisense oligonucleotide that induces survival motor neuron (SMN) protein expression, it was approved by the U.S. FDA in December, 2016 as Spinraza for the treatment of children and adults with spinal muscular atrophy (SMA). It is adminstrated as direct intrathecal injection.

Accession Number
DBSALT002592
Synonyms
Not Available
UNII
4CHB7QQU1Q
CAS Number
Not Available
Wikipedia
Nusinersen