Hydrolytic Lysosomal Glycogen-specific Enzyme
- Hydrolytic Lysosomal Glycogen-specific Enzyme
- Accession Number
Drug Drug Description Alglucosidase alfa An acid alpha- glucosidase (GAA) derivative used as an enzyme replacement therapy for the treatment of Pompe disease in infants and pediatric patients caused by GAA deficiency. Avalglucosidase alfa A lysosomal glycogen-specific enzyme that is used to treat patients one year of age and older with late-onset Pompe disease, or lysosomal acid alpha-glucosidase (GAA) deficiency.
- Drugs & Drug Targets
Drug Target Type Alglucosidase alfa Cation-dependent mannose-6-phosphate receptor target Alglucosidase alfa Glycogen target Avalglucosidase alfa Cation-independent mannose-6-phosphate receptor target