Mucopolysaccharidosis Type I (MPS I)

DBCOND0065667Congenital, Hereditary, and Neonatal Diseases and AbnormalitiesNutritional and Metabolic Diseases

Mucopolysaccharidosis Type I (MPS I) is the indication for 1 drug in DrugBank. It is covered by 3 curated, structured indications.

Also known as
Mucopolysaccharidosis I · Type 1 Mucopolysaccharidosis · Mucopolysaccharidosis Type I · Dysostosis Multiplex · Gargoylism
Classified under
Indicated drugs

Resolves to

Vocabularies
MeSHM0012558ICD-10E76.0SNOMED CT190936000MedDRA10020470UMLSC0023786

What you can answer from here — as of October 30, 2026

1Indicated drugWith each drug's targets and mechanism
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3Structured indicationsPopulation, line of therapy, route and combination as fields, not prose
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56Clinical trialsPhase, status and sponsor resolved per trial
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Which approved drugs for Mucopolysaccharidosis Type I (MPS I) share a target, and which companies have late-stage candidates against it?

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