Acid Cholesteryl Ester Hydrolase Deficiency, Wolman Type

DBCOND0076044Congenital, Hereditary, and Neonatal Diseases and Abnormalities Digestive System Diseases

Acid Cholesteryl Ester Hydrolase Deficiency, Wolman Type is the indication for 1 drug in DrugBank. It is covered by 1 curated, structured indication.

Also known as: Lysosomal Acid Lipase Deficiency · Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 · Acid Lipase Deficiency
Classified under: Congenital, Hereditary, and Neonatal Diseases and Abnormalities
Digestive System Diseases
Nutritional and Metabolic Diseases
Pregnancy, Puerperium, and Perinatal Conditions
Indicated drugs: Sebelipase alfa

Resolves to

Vocabularies

MeSHM0525345ICD-10E75.5SNOMED CT190795007MedDRA10053687UMLSC0043208

What you can answer from here — as of October 22, 2026

1Indicated drugWith each drug's targets and mechanism

Listed above

1Structured indicationPopulation, line of therapy, route and combination as fields, not prose

7Clinical trialsPhase, status and sponsor resolved per trial

1Drug reporting it as an adverse effectWith incidence where the label states it

Which approved drugs for Acid Cholesteryl Ester Hydrolase Deficiency, Wolman Type share a target, and which companies have late-stage candidates against it?

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