Mucopolysaccharidosis IIIA

DBCOND0086409Genetic Diseases, InbornNutritional and Metabolic Diseases

Mucopolysaccharidosis IIIA is the indication for 1 drug in DrugBank. It is covered by 1 curated, structured indication.

Also known as
Sanfilippo Syndrome Type A · Sanfilippo Syndrome Type A (MPS IIIA) · Mucopolysaccharidosis Type III A · Sanfilippo Disease Type A · Mucopolysaccharidosis Type IIIA
Classified under
Indicated drugs

Resolves to

Vocabularies
MeSHT783003ICD-10E76.22SNOMED CT254070003UMLSC0086647

What you can answer from here — as of October 23, 2026

1Indicated drugWith each drug's targets and mechanism
Listed above
1Structured indicationPopulation, line of therapy, route and combination as fields, not prose
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12Clinical trialsPhase, status and sponsor resolved per trial
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Which approved drugs for Mucopolysaccharidosis IIIA share a target, and which companies have late-stage candidates against it?

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