Acid Sphingomyelinase Deficiency (ASMD)

DBCOND0147964Central Nervous System DisorderCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Acid Sphingomyelinase Deficiency (ASMD) is the indication for 1 drug in DrugBank. It is covered by 2 curated, structured indications.

Also known as
Acid Sphingomyelinase Deficiency · Human Acid Sphingomyelinase Deficiency
Classified under
Indicated drugs

Resolves to

Vocabularies
MeSHT001124733ICD-10E75.24SNOMED CT58459009MedDRA10029403UMLSC0028064

What you can answer from here — as of October 22, 2026

1Indicated drugWith each drug's targets and mechanism
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2Structured indicationsPopulation, line of therapy, route and combination as fields, not prose
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5Clinical trialsPhase, status and sponsor resolved per trial
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1Drug reporting it as an adverse effectWith incidence where the label states it
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Which approved drugs for Acid Sphingomyelinase Deficiency (ASMD) share a target, and which companies have late-stage candidates against it?

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