DB16264InvestigationalGene Therapies
Olenasufligene relduparvovec is under investigation in clinical trial NCT03612869 (Study of aavrh10-h.sgsh Gene Therapy in Patients With Mucopolysaccharidosis Type IIIA (MPS IIIA)). It is an adeno-associated virus (AAV) vector that...
- Also known as
- AAVrh10-h.SGSH · Aavrh10-hsgsh · Dna (recombinant adeno-associated virus 2 vector lys-saf302 human n-sulfoglucosamine sulfohydrolase cdna-specifying)
- Code names
- LYS-SAF-302 · SRP-9002
Resolves to
Compound
What you can answer from here — as of April 23, 2025
Which companies are running trials of Olenasufligene relduparvovec, in which indications and phases, and which of those programs are still active?
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