DB16785InvestigationalGene Therapies
Volrubigene ralaparvovec is under investigation in clinical trial NCT03223194 (Gene Transfer Clinical Study in Crigler-najjar Syndrome).
- Also known as
- Non-replicating recombinant adeno-associated viral vector, serotype 8, expressing the 1A1 isoform of the bilirubin-uridine diphosphate glucuronosyltransferase gene
- Code names
- AT-003 · AT-342
Resolves to
Compound
What you can answer from here — as of September 25, 2025
Which companies are running trials of Volrubigene ralaparvovec, in which indications and phases, and which of those programs are still active?
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