DB16814InvestigationalGene Therapies
Botaretigene sparoparvovec: Overview.
- Also known as
- AAV5-hRKp.RPGR · AAV5-RPGR · DNA (RECOMBINANT PSEUDOTYPED ADENO-ASSOCIATED VIRUS 5 VECTOR AAV-RPGR HUMAN RHODOPSIN KINASE PROMOTER FRAGMENT-REGULATED HUMAN RETINITIS PIGMENTOSA GTPASE REGULATOR RPGR-ORF15 ISOFORM GENE VARIANT PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMINAL REPEAT FL
- Code names
- AAV-RPGR
Resolves to
Compound
What you can answer from here — as of November 21, 2025
Which companies are running trials of Botaretigene sparoparvovec, in which indications and phases, and which of those programs are still active?
Create a free account or log in to explore the full data card.
Create Account