Vesleteplirsen

DB16993InvestigationalGene Therapies

Vesleteplirsen: Overview.

Mechanism: Pharmacologically active on DMD-001 gene (exon 51 target site)
Curator reviewed
Code names: SRP-5051

Resolves to

Compound

What you can answer from here — as of October 05, 2026

1Protein targetEach mapped to UniProt, with action and pharmacological action

Listed above

3Clinical trialsPhase, status and sponsor resolved per trial

3+ReferencesStructured and connected to the statements they support

Which companies are running trials of Vesleteplirsen, in which indications and phases, and which of those programs are still active?

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