DB17632Investigational
RGX-111 is an adeno-associated virus vector AAV9 designed to deliver the α-L-iduronidase (IDUA) gene. Developed by REGENXBIO Inc., it was investigated for the treatment of mucopolysaccharidosis Type I (MPS I).
- Also known as
- Adeno-associated virus vector serotype 9 expressing human a-L-iduronidase
- Code names
- RGX-111
What you can answer from here — as of September 25, 2025
Which companies are running trials of RGX-111, in which indications and phases, and which of those programs are still active?
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