DB17646InvestigationalGene Therapies
VTX-801 is a replication-deficient recombinant adeno-associated viral vector (rAAV) consisting of an AAV liver tropic capsid containing a single-stranded DNA genome carrying a shortened version of the ATP7B gene (ATP7B-minigene).... It is being investigated in Wilson Disease.
- Code names
- VTX-801
Resolves to
Compound
What you can answer from here — as of September 25, 2025
Which companies are running trials of VTX-801, in which indications and phases, and which of those programs are still active?
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