DB17681InvestigationalGene Therapies
RGX-121 is designed to use the NAV AAV9 vector to deliver the human iduronate-2-sulfatase gene to the central nervous system.
- Code names
- RGX-121
Resolves to
Compound
What you can answer from here — as of November 27, 2025
Which companies are running trials of RGX-121, in which indications and phases, and which of those programs are still active?
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