DB17943ExperimentalGene Therapies
AVXS-301 consists of an adeno-associated virus serotype 9 (AAV9) designed to express the superoxide dismutase 1 (SOD1) gene. It is being investigated for the treatment of Amyotrophic Lateral Sclerosis (ALS).
- Also known as
- AVXS 301 · AVXS301
- Code names
- OAV-301
What you can answer from here — as of March 06, 2025
Which companies are running trials of AVXS-301, in which indications and phases, and which of those programs are still active?
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