DB18138InvestigationalGene Therapies
PBKR03 is a non-replicating recombinant adeno-associated virus serotype hu68 vector, containing a transgene encoding the human galactosylceramidase (GALC) enzyme.
- Code names
- PBKR03
What you can answer from here — as of April 23, 2025
Which companies are running trials of PBKR03, in which indications and phases, and which of those programs are still active?
Create a free account or log in to explore the full data card.
Create Account