GS-100

DB18337InvestigationalGene Therapies

GS-100 is an adeno-associated virus serotype 9 virus particle containing viral DNA that includes an expression cassette containing the human NGLY1 gene coding sequence.

Code names
GS-100

What you can answer from here — as of May 11, 2026

1Clinical trialPhase, status and sponsor resolved per trial
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Which companies are running trials of GS-100, in which indications and phases, and which of those programs are still active?

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