DB18631ExperimentalCell transplant therapies
AVR-RD-05 is a gene therapy comprising genetically modified autologous stem cells transduced ex vivo with a lentiviral vector encoding the human iduronate-2-sulfatase (IDS) enzyme. It is under investigation for the... It is under investigation for the treatment of Hunter Syndrome (Mucopolysaccharidosis Type II, MPSII).
- Code names
- AVR-RD-05
Which companies are running trials of AVR-RD-05, in which indications and phases, and which of those programs are still active?
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