DB18644ExperimentalCell transplant therapies
AVR-RD-04 is an investigational gene therapy for cystinosis. It consists of autologous CD34+ enriched cells transduced with a lentiviral vector containing RNA resulting in codon-optimized cDNA encoding for functional human...
- Also known as
- autologous CD34+ enriched cells transduced with a lentiviral vector containing RNA resulting in codon-optimized cDNA encoding for functional human cystinosin
- Code names
- AVR-RD-04
Which companies are running trials of AVR-RD-04, in which indications and phases, and which of those programs are still active?
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