Rett's Syndrome

Also known as: Rett Syndrome / Rett's Disorder / RTT / Rett Disorder / Rett's disorder (disorder)

DrugDrug NameDrug Description
DB06045TrofinetideA drug used to treat Rett syndrome in children and adults.
DrugDrug NamePhaseStatusCount
DB11823Esketamine0Recruiting1
DB05259Glatiramer1Unknown Status1
DB16956L-Acetylleucine1Completed1
DB01277Mecasermin1Completed1
DB08868Fingolimod1 / 2Completed1
DB05592Blarcamesine2Completed1
DB01151Desipramine2Completed1
DB00514Dextromethorphan2Completed1
DB00514Dextromethorphan2Terminated1
DB05259Glatiramer2Completed1
DB00030Insulin human2Completed1
DB01221Ketamine2Completed1
DB00227Lovastatin2Completed1
DB01277Mecasermin2Completed1
DB11677Triheptanoin2Unknown Status2
DB06045Trofinetide2Completed2
DB11917Vatiquinone2Completed1
DB05592Blarcamesine2 / 3Completed1
DB00936Salicylic acid2 / 3Completed1
DB06454Sarizotan2 / 3Terminated1
DB06045Trofinetide2 / 3Completed1
DB05592Blarcamesine3Completed1
DB09061Cannabidiol3Terminated2
DB00514Dextromethorphan3Unknown Status1
DB00843Donepezil3Unknown Status1
DB00734Risperidone3Completed1
DB06045Trofinetide3Completed3
DB00514DextromethorphanNot AvailableCompleted1
DB00843DonepezilNot AvailableCompleted1
DB00273TopiramateNot AvailableCompleted1