Rett Syndrome

Rett Syndrome is the indication for 1 drug in DrugBank. It is covered by 3 curated, structured indications.

Also known as: Rett's Disorder · Rett's Syndrome · RTT
Classified under: Congenital, Hereditary, and Neonatal Diseases and Abnormalities
Mental Disorders
Mutations
Nervous System Diseases
Nutritional and Metabolic Diseases
Pathological Processes
Indicated drugs: Trofinetide

Resolves to

Vocabularies

MeSHM0023877ICD-10F84.2SNOMED CT192583003MedDRA10039000UMLSC0035372

What you can answer from here — as of October 09, 2026

1Indicated drugWith each drug's targets and mechanism

Listed above

3Structured indicationsPopulation, line of therapy, route and combination as fields, not prose

52Clinical trialsPhase, status and sponsor resolved per trial

1Drug reporting it as an adverse effectWith incidence where the label states it

Which approved drugs for Rett Syndrome share a target, and which companies have late-stage candidates against it?

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