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Devafidugene civaparvovec
go.drugbank.com/drugs/DB16790InvestigationalIt uses proprietary zinc finger nucleases (ZFN) that insert a functional copy of the alpha-L-iduronidase (IDUA) enzyme. … Developed by Sangamo Therapeutics, Inc., devafidugene civaparvovec is being investigated for the treatment of mucopolysaccharidosis Type I (MPS I).[L46716]
Isaralgagene civaparvovec
go.drugbank.com/drugs/DB16808InvestigationalIsaralgagene civaparvovec, formerly known as ST-920, is liver-tropic rAAV 2/6 vector carrying the cDNA for human alpha-galactosidase A (α-Gal A) enzyme.
S-49076
go.drugbank.com/drugs/DB16821ExperimentalCategories: Heterocyclic Compounds, 1-Ring, Heterocyclic Compounds, 2-RingCinchonidine
go.drugbank.com/drugs/DB16831ExperimentalSynonyms: Quinine bisulfate impurity B, Quinine sulfate impurity BCategories: Cytochrome P-450 CYP2D6 Inhibitors, Cytochrome P-450 Enzyme InhibitorsBentamapimod
go.drugbank.com/drugs/DB16851InvestigationalCategories: Heterocyclic Compounds, 1-Ring, Heterocyclic Compounds, 2-RingTyrosol
go.drugbank.com/drugs/DB16855ExperimentalSynonyms: p-Tyrosol, 4-HydroxyphenylethanolCategories: Cytochrome P-450 Substrates, Cytochrome P-450 CYP2A6 SubstratesIndigo
go.drugbank.com/drugs/DB16862InvestigationalSynonyms: D&C Blue No. 6Categories: Heterocyclic Compounds, 2-Ring, Compounds used in a research, industrial, or household settingCB-5083
go.drugbank.com/drugs/DB16874InvestigationalSynonyms: 1-(4-(benzylamino)-7,8-dihydro-5H-pyrano[4,3-d]pyrimidin-2-yl)-2-methyl-1H-indole-4-carboxamide, 1-(7,8-Dihydro-4-((phenylmethyl)amino)-5H-pyrano(4,3-d)pyrimidin-2-yl)-2-methyl-1H-indole-4-carboxamideCategories: Heterocyclic Compounds, 1-Ring, Heterocyclic Compounds, 2-Ring