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EF-022
go.drugbank.com/drugs/DB17768InvestigationalEF-022 is a modified version of vitamin D binding protein macrophage activator, with potential antineoplastic and anti-angiogenic activities.
Synonyms: Modified vitamin D binding protein, Modified Vitamin D Binding Protein Macrophage ActivatorOctovalent O-polysaccharide-toxin A conjugate vaccine
go.drugbank.com/drugs/DB17789ExperimentalOctovalent O-polysaccharide-toxin A conjugate vaccine is currently being investigated to treat Pseudomonas Aeruginosa infection in patients with cystic fibrosis.[A259462]
Synonyms: Octovalent O-polysaccharide-toxin A conjugate vaccine, octavalent Psuedomonas aeruginosa O-polysaccaharide-toxin A conjugateN-9-Methoxynonyldeoxynojirimycin
go.drugbank.com/drugs/DB17804ExperimentalSynonyms: 3,4,5-piperidinetriol, 2-(hydroxymethyl)-1-(9-methoxynonyl)-, (2r,3r,4r,5s)-Salts: N-9-Methoxynonyldeoxynojirimycin hydrochlorideAGA2115
go.drugbank.com/drugs/DB17840InvestigationalAGA2115 is a humanized bispecific antibody neutralizing both sclerostin and Dickkopf-1.
CDX-6512
go.drugbank.com/drugs/DB17841ExperimentalCDX-6512 is a modified, gastrointestinal-stable bacterial leucine decarboxylase. Developed by Codexis, it is being investigated for the treatment of homocystinuria And Maple Syrup Urine Disease.
Sonpiretigene isteparvovec
go.drugbank.com/drugs/DB17844Investigational[L46676] Sonpiretigene isteparvovec consists of a fusion Adeno-associated virus (AAV) vector with three plasmids encoding opsins with spectrally-separated activation peaks.[L46681]
Synonyms: VMCO-1, vMCO-ISPL23-2
go.drugbank.com/drugs/DB17866ExperimentalSPL23-2 is an antisense oligonucleotide (ASO) targeting the W1282X nonsense mutation associated with a severe form of cystic fibrosis.[L46767]
Bacteroides thetaiotaomicron
go.drugbank.com/drugs/DB17879InvestigationalBacteroides thetaiotaomicron is a live biotherapeutic.
NGGT-002
go.drugbank.com/drugs/DB17881InvestigationalNGGT-002 is a recombinant adeno-associated virus serotype 8 vector encoding human phenylalanine hydroxylase (PAH).
GT-AS
go.drugbank.com/drugs/DB17883ExperimentalGT-AS recombinant adeno-associated virus serotype 9 vector containing the transgene UBE3A encoding for ubiquitin protein ligase E3A/E6-AP.