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Displaying results 9271 - 9280 of 10000 in total
  1. Drug

    PRX-OTC

    go.drugbank.com/drugs/DB17680
    Experimental

    PRX-OTC is an intracellular enzyme replacement therapy designed to replace missing or defective enzyme in patients with ornithine transcarbamylase deficiency.

  2. Drug

    Dalcinonacog alfa

    go.drugbank.com/drugs/DB17707
    Investigational

    It is being investigated for the treatment of hemophilia B.[A259058]

  3. Drug

    SPL23-2

    go.drugbank.com/drugs/DB17866
    Experimental

    SPL23-2 is an antisense oligonucleotide (ASO) targeting the W1282X nonsense mutation associated with a severe form of cystic fibrosis.[L46767]

  4. Drug

    OTOF-GT

    go.drugbank.com/drugs/DB18129
    Investigational

    OTOF-GT is a dual vector AAV gene therapy being investigated for the restoration of hearing loss associated with otoferlin deficiency.

  5. Drug

    TTX-MC138

    go.drugbank.com/drugs/DB18628
    Investigational

    [L48335] It is under investigation for the treatment of various metastatic cancers.

  6. Drug

    Rulonilimab

    go.drugbank.com/drugs/DB18922
    Investigational

    Rulonilimab is under investigation in clinical trial NCT05408221 (The Efficacy and Safety of Rulonilimab in Combination With Lenvatinib in Hepatocellular Carcinoma).

  7. Drug

    Pirmitegravir

    go.drugbank.com/drugs/DB18974
    Investigational

    Pirmitegravir is under investigation in clinical trial NCT05869643 (A Clinical Trial of STP0404 in Treatment-naïve Adults With HIV-1 Infection).

  8. Drug

    Pegtarviliase

    go.drugbank.com/drugs/DB18999
    Investigational

    Pegtarviliase is under investigation in clinical trial NCT05154890 (A Multiple Ascending Dose Study of ACN00177 (Pegtarviliase) in Subjects With CBS Deficiency).

  9. Drug

    Atuzaginstat

    go.drugbank.com/drugs/DB19030
    Investigational

    Atuzaginstat is under investigation in clinical trial NCT03823404 (GAIN Trial: Phase 2/3 Study of COR388 in Subjects With Alzheimer's Disease).

  10. Drug

    Kisspeptin

    go.drugbank.com/drugs/DB19112
    Investigational

    Kisspeptin is under investigation in clinical trial NCT03315325 (Age-dependent Changes in the Responsiveness of Hypothalamic Pituitary Gonadal Axis in Men).