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Eladocagene exuparvovec

go.drugbank.com/drugs/DB16780
ApprovedInvestigational

Eladocagene exuparvovec is a recombinant adeno-associated virus-2 (AAV2)-based gene therapy that expresses human aromatic L-amino acid decarboxylase (AADC), and it is used to treat AADC deficiency, a fatal and rare genetic disorder that causes severe disability in pediatric patients. Patients with AADC have mutation...

  1. Indication

    Aromatic L-amino Acid Decarboxylase (AADC) Deficiency

    go.drugbank.com/conditions/DBCOND0053491
    Drugs: Eladocagene exuparvovec