Aminolevulinate Synthase 1-Directed Small Interfering RNAs

Name
Aminolevulinate Synthase 1-Directed Small Interfering RNAs
Accession Number
DBCAT005670
Description

RNA interference therapies that inhibit aminolevulinate synthase-1 expression.

Drugs
DrugDrug Description
GivosiranA 5-aminolevulinic acid synthase-directed small interfering RNA (siRNA) used in the prophylaxis of acute hepatic porphyria.
Drugs & Drug Targets
DrugTargetType
GivosiranALAS1 mRNAtarget