DB17867InvestigationalGene Therapies
QR-313 is an antisense oligonucleotide targeting exon 73. It is being investigated for the treatment of dystrophic epidermolysis bullosa.
- Mechanism
- Curator reviewed
Pharmacologically active on Collagen alpha-1(VII) chain
- Also known as
- PTW-002 · QRX-313
- Code names
- QR-313
Resolves to
Targets
What you can answer from here — as of October 05, 2026
Which drugs share a target with QR-313, and which of those have an active Phase 3 trial?
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