QR-313

DB17867InvestigationalGene Therapies

QR-313 is an antisense oligonucleotide targeting exon 73. It is being investigated for the treatment of dystrophic epidermolysis bullosa.

Also known as
PTW-002 · QRX-313
Code names
QR-313

What you can answer from here — as of April 23, 2025

2Clinical trialsPhase, status and sponsor resolved per trial
Sign in
1+ReferenceStructured and connected to the statements they support
Sign in

Which companies are running trials of QR-313, in which indications and phases, and which of those programs are still active?

Create a free account or log in to explore the full data card.

Create Account