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Displaying results 5031 - 5040 of 10000 in total
  1. Drug

    N-9-Methoxynonyldeoxynojirimycin

    go.drugbank.com/drugs/DB17804
    Experimental

    Salts: N-9-Methoxynonyldeoxynojirimycin hydrochlorideCategories: Heterocyclic Compounds, 1-Ring
  2. Drug

    Ultevursen

    go.drugbank.com/drugs/DB17835
    Investigational

    Ultevursen is a single-stranded RNA-based oligonucleotide targeting exon 13 of the USH2A gene that encodes usherin.

  3. Drug

    AGA2115

    go.drugbank.com/drugs/DB17840
    Investigational

    AGA2115 is a humanized bispecific antibody neutralizing both sclerostin and Dickkopf-1.

  4. Drug

    CDX-6512

    go.drugbank.com/drugs/DB17841
    Experimental

    CDX-6512 is a modified, gastrointestinal-stable bacterial leucine decarboxylase. Developed by Codexis, it is being investigated for the treatment of homocystinuria And Maple Syrup Urine Disease.

  5. Drug

    Sonpiretigene isteparvovec

    go.drugbank.com/drugs/DB17844
    Investigational

    [L46676] Sonpiretigene isteparvovec consists of a fusion Adeno-associated virus (AAV) vector with three plasmids encoding opsins with spectrally-separated activation peaks.[L46681]

    Synonyms: VMCO-1, vMCO-I
  6. Drug

    BAX 335

    go.drugbank.com/drugs/DB17845
    Investigational

    BAX 335 is an adeno-associated virus vector 8 (AAV8)–based FIX gene therapy being investigated for the treatment of hemophilia B.[A259791]

    Synonyms: An Adeno-Associated Virus Serotype 8 (AAV8) Vector Expressing FIX Padua (AAV8.ss-3xCRM8-TTRFIX_R338Lopt)
  7. Drug

    AAV-AIPL

    go.drugbank.com/drugs/DB17857
    Experimental

    AAV-AIPL is an adenovirus-associated viral vector serotype 8 containing the human _AIPL1_ gene.

    Synonyms: adenovirus associated viral vector serotype 8 containing the human AIPL1 gene
  8. Drug

    SPL23-2

    go.drugbank.com/drugs/DB17866
    Experimental

    SPL23-2 is an antisense oligonucleotide (ASO) targeting the W1282X nonsense mutation associated with a severe form of cystic fibrosis.[L46767]

  9. Drug

    Bacteroides thetaiotaomicron

    go.drugbank.com/drugs/DB17879
    Investigational

    Bacteroides thetaiotaomicron is a live biotherapeutic.

  10. Drug

    NGGT-002

    go.drugbank.com/drugs/DB17881
    Investigational

    NGGT-002 is a recombinant adeno-associated virus serotype 8 vector encoding human phenylalanine hydroxylase (PAH).