Ultevursen

DB17835InvestigationalNucleic Acid Based Therapies

Ultevursen is a single-stranded RNA-based oligonucleotide targeting exon 13 of the USH2A gene that encodes usherin. It was developed by ProQR Therapeutics and is being investigated for the treatment of...

Mechanism: Pharmacologically active on Usherin
Curator reviewed
Code names: QR-421 · QR-421a · QRX-421

Resolves to

Compound

UNII94AC8YWE3ICAS2642382-41-8

Targets

O75445USH2A

What you can answer from here — as of July 08, 2026

1Protein targetEach mapped to UniProt, with action and pharmacological action

Listed above

5Clinical trialsPhase, status and sponsor resolved per trial

5+ReferencesStructured and connected to the statements they support

Which drugs share a target with Ultevursen, and which of those have an active Phase 3 trial?

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