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AAV1-FS344
go.drugbank.com/drugs/DB17855InvestigationalAAV1-FS344 is an investigational gene therapy developed by Milo Biotechnology to deliver follistatin, a potent myostatin inhibitor. … It is being investigated for the treatment of Duchenne Muscular Dystrophy, Becker Muscular Dystrophy, and inclusion body myositis.[L46742, L46747, L46752]
SOBI-003
go.drugbank.com/drugs/DB15451InvestigationalSOBI-003 is a chemically modified variant of a recombinant human sulfamidase. … It is under investigation in clinical trial NCT03811028 (A Study to Assess the Safety, Tolerability, and Efficacy of Long-term SOBI003 Treatment in Pediatric MPS IIIA Patients).
Flurocitabine
go.drugbank.com/drugs/DB20317ExperimentalFlurocitabine is a small molecule drug. … The usage of the INN stem '-citabine' in the name indicates that Flurocitabine is a nucleoside antiviral or antineoplastic agent, cytarabine or azacitidine derivative.
Synonyms: 5-fluorocyclocytidine, 5'-fluorocyclocytidineAderbasib
go.drugbank.com/drugs/DB21288InvestigationalAderbasib is a small molecule drug. … Aderbasib has a monoisotopic molecular weight of 416.21 Da.
Acloproxalap
go.drugbank.com/drugs/DB21553InvestigationalAcloproxalap is a small molecule drug. … Acloproxalap is under investigation in clinical trial NCT06685692 (A Clinical Trial Investigating the Safety and Efficacy of Subjects With Alcohol Associated Hepatitis (Part 1)).
Categories: Heterocyclic Compounds, 2-RingPlazinemdor
go.drugbank.com/drugs/DB21493InvestigationalPlazinemdor is a small molecule drug. Plazinemdor is under investigation in clinical trial NCT04306146 (Study of CAD-9303 in Subjects With Schizophrenia). … Plazinemdor has a monoisotopic molecular weight of 432.12 Da.
Tirfipiravir
go.drugbank.com/drugs/DB21648ExperimentalTirfipiravir is a small molecule drug. The usage of the INN stem '-vir' in the name indicates that Tirfipiravir is a antiviral. Tirfipiravir has a monoisotopic molecular weight of 355.1 Da.
tgAAVCF
go.drugbank.com/drugs/DB17849InvestigationalIt is being investigated for the treatment of cystic fibrosis.[A259821, A259826] … tgAAVCF is an adeno-associated virus (AAV) vector encoding the human cystic fibrosis transmembrane conductance regulator protein (CFTR) cDNA.
Clometherone
go.drugbank.com/drugs/DB19465ExperimentalClometherone is a small molecule drug. The usage of the INN stem '-terone' in the name indicates that Clometherone is a antiandrogen. Clometherone has a monoisotopic molecular weight of 362.2 Da.
Derquantel
go.drugbank.com/drugs/DB19531ExperimentalDerquantel is a small molecule drug. The usage of the INN stem '-antel' in the name indicates that Derquantel is a anthelminthic. Derquantel has a monoisotopic molecular weight of 479.28 Da.
Categories: Heterocyclic Compounds, 1-Ring, Heterocyclic Compounds, 2-Ring