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PBKR03
go.drugbank.com/drugs/DB18138InvestigationalPBKR03 is a non-replicating recombinant adeno-associated virus serotype hu68 vector, containing a transgene encoding the human galactosylceramidase (GALC) enzyme.
TN-401
go.drugbank.com/drugs/DB18140InvestigationalTN-401 is a native AAV9 capsid with a genomic cassette containing a cardiomyocyte-specific promoter and the wild-type human PKP2 gene.
Synonyms: A native AAV9 capsid with a genomic cassette containing a cardiomyocyte-specific promoter and the wild-type human PKP2 geneEfocipegtrutide
go.drugbank.com/drugs/DB18194InvestigationalEfocipegtrutide is a long-acting, monomeric peptide triple agonist.
XMT-2056
go.drugbank.com/drugs/DB18230InvestigationalXMT-2056 is a HER2-targeted antibody-drug conjugate (ADC) consisting of a HER2-targeted antibody conjugated with a stimulator of interferon genes (STING) agonist payload.
AP103
go.drugbank.com/drugs/DB18234ExperimentalAP103 is a non-viral gene therapy that uses a delivery vector, HPAE (Highly Branched Poly β-Amino Ester), to deliver the correct collagen VII gene into skin cells.
DCN-tCRK
go.drugbank.com/drugs/DB18262ExperimentalDCN-tCRK is a recombinant, multi-functional fusion protein consisting of human decorin fused to the C-terminal vascular homing peptide tCRK.
HM15912
go.drugbank.com/drugs/DB18266InvestigationalHM15912 is a human glucagon-like peptide-2 analogue linked to a human immunoglobulin Fc fragment.
TLY-012
go.drugbank.com/drugs/DB18336ExperimentalTLY-012 is a PEGylated recombinant human tumor necrosis factor-related apoptosis-inducing ligand (PEGylated TRAIL).[L48166]
EB003
go.drugbank.com/drugs/DB18362ExperimentalEB003 is a CRISPR-based sequence-specific antimicrobial (SSAM) targeted against shiga toxin-producing _E. coli_.
Synonyms: Phage-derived, non-replicative delivery vector carrying a DNA payload encoding an RNA-guided nuclease that targets stx genes of Shiga toxin-producing Escherichia coli (STEC)MDX-1097
go.drugbank.com/drugs/DB18383ExperimentalMDX-1097 is a chimeric monoclonal antibody directed against the kappa myeloma antigen (KMA).