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Displaying results 1 - 10 of 12 in total
Growth Hormone Gene Deletion
go.drugbank.com/conditions/DBCOND0118367Drugs: Mecasermin rinfabateSynonyms: Growth Hormone Gene DeletionOtoferlin Gene-mediated Hearing Loss
go.drugbank.com/conditions/DBCOND0170571Drugs: Lunsotogene parvecSynonyms: Otoferlin Gene-mediated Hearing Loss, Congenital Hearing Loss Secondary to Biallelic Mutations in the Otoferlin Gene (OTOF)HRR gene-mutated (HRRm) metastatic castration-resistant prostate cancer (mCRPC)
go.drugbank.com/conditions/DBCOND0159058Drugs: TalazoparibSynonyms: HRR gene-mutated (HRRm) metastatic castration-resistant prostate cancer (mCRPC)Hematopoietic Subsyndrome of Acute Radiation Syndrome
go.drugbank.com/conditions/DBCOND0020289Synonyms: H-ARS - Hematopoietic subsyndrome of acute radiation syndrome, H-ARS - Haematopoietic subsyndrome of acute radiation syndromeHyperargininemia
go.drugbank.com/conditions/DBCOND0002645Drugs: PegzilarginaseSynonyms: ARG1-gene related arginase deficiency, Arginase 1-gene related arginase deficiencyArgininosuccinate Synthetase Deficiency (Citrullinemia)
go.drugbank.com/conditions/DBCOND0078378Drugs: Phenylbutyric acidSynonyms: ASS1-gene related citrullinemia type I, ASS1-gene related citrullinaemia type ITyrosinemia Type 1
go.drugbank.com/conditions/DBCOND0091509Drugs: NitisinoneSynonyms: FAH-gene related tyrosinemia type 1, FAH-gene related tyrosinaemia type 1Respiratory Distress Syndrome
go.drugbank.com/conditions/DBCOND0027916Synonyms: ARDS, ARDS - Adult respiratory distress syndromeCongenital carnitine deficiency
go.drugbank.com/conditions/DBCOND0008341Drugs: LevocarnitineSynonyms: SLC22A5-gene related renal carnitine transport defectCarbamyl Phosphate Synthetase Deficiency
go.drugbank.com/conditions/DBCOND0051997Drugs: Phenylbutyric acidSynonyms: CPS1-gene related carbamoyl-phosphate synthetase 1 deficiency