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Fitusiran
go.drugbank.com/drugs/DB15002
ApprovedInvestigational
Fitusiran is an antithrombin-directed double-stranded small interfering ribonucleic acid (siRNA) that is covalently linked to a ligand containing a triantennary N-acetylgalactosamine (GalNAc) moiety. Fitusiran was first approved by the FDA on March 28, 2025, as routine prophylaxis therapy to prevent or reduce the fr...
Bleeding caused by Hemophilia B Without Inhibitor
go.drugbank.com/conditions/DBCOND0170628Bleeding caused by Hemophilia A Without Inhibitor
go.drugbank.com/conditions/DBCOND0170627Bleeding caused by Hemophilia B
go.drugbank.com/conditions/DBCOND0089514Bleeding caused by Hemophilia A
go.drugbank.com/conditions/DBCOND0089512