Familial Amyloid Polyneuropathy (FAP) (DBCOND0071574)

Identifiers

Synonyms

Familial Amyloid Polyneuropathies / Familial Amyloid Polyneuropathy / Hereditary neuropathic amyloidosis / Neuropathic heredofamilial amyloidosis / Amyloid Neuropathies, Familial / Familial amyloid polyneuropathy (disorder)

Associated Data

Indicated Drugs and Targets

Not Available

Clinical Trials

Identifier	Title	Drug(s)	Purpose	Phase	Status
NCT01960348	APOLLO: The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis	Patisiran	treatment	3	completed
NCT02939820	Expanded Access Protocol of Patisiran for Patients With Hereditary ATTR Amyloidosis (hATTR)	Patisiran	Not Available	Not Available	approved_for_marketing
NCT02191826	Study of SOM0226 in Familial Amyloid Polyneuropathy	No drug interventions	treatment	1 / 2	completed
NCT01737398	Efficacy and Safety of Inotersen in Familial Amyloid Polyneuropathy	Inotersen	treatment	2 / 3	completed
NCT00294671	The Effect of Diflunisal on Familial Amyloidosis	Diflunisal	treatment	2 / 3	completed
NCT00409175	Safety and Efficacy Study of Fx-1006A in Patients With Familial Amyloidosis	Fx-1006A	treatment	2 / 3	completed
NCT00791492	An Extension of Study Fx-005 Evaluating Long-Term Safety And Clinical Outcomes Of Fx-1006A In Patients With Transthyretin Amyloid Polyneuropathy	Fx-1006A	treatment	2 / 3	completed
NCT02175004	Extension Study Assessing Long Term Safety and Efficacy of IONIS-TTR Rx in Familial Amyloid Polyneuropathy (FAP)	Inotersen	treatment	3	completed