X-Linked Adrenoleukodystrophy (X-ALD) (DBCOND0086724)
Identifiers
- Synonyms
- X-Linked Adrenoleukodystrophy / X-linked adrenoleukodystrophy, unspecified type / Adrenoleukodystrophy / Adrenoleukodystrophy (disorder)
Associated Data
- Indicated Drugs and Targets
- Not Available
- Clinical Trials
Identifier Title Drug(s) Purpose Phase Status NCT02698579 Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product No drug interventions Not Available Not Available active_not_recruiting NCT02204904 Observational Study to Evaluate Allogeneic HSCT Outcomes for Cerebral Adrenoleukodystrophy (CALD) No drug interventions Not Available Not Available terminated NCT02699190 LeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies No drug interventions Not Available Not Available active_not_recruiting NCT05939232 Registry of X-linked Adrenoleukodystrophy No drug interventions Not Available Not Available recruiting NCT03278899 A Study to Prospectively Assess Disease Progression in Male Children With X-ALD No drug interventions Not Available Not Available unknown_status NCT02233257 Expanded Access for Lorenzo's Oil (GTO/GTE) in Adrenoleukodystrophy Not Available Not Available no_longer_available NCT03196765 Safety, Pharmacokinetics and Pharmacodynamics of NV1205 in Pediatric Male Subjects With Adrenoleukodystrophy treatment 1 / 2 withdrawn NCT06178120 Disease Progression in Women With X-linked Adrenoleukodystrophy No drug interventions Not Available Not Available recruiting NCT03047369 The Myelin Disorders Biorepository Project No drug interventions Not Available Not Available recruiting NCT03864523 Effect of Pioglitazone Administered to Patients With Adrenomyeloneuropathy treatment 2 completed NCT01594853 Exercise Study of Function and Pathology for Women With X-linked Adrenoleukodystrophy No drug interventions treatment Not Available completed NCT01787578 Safety and Pharmacodynamic Study of Sobetirome in X-Linked Adrenoleukodystrophy (X-ALD) treatment 1 withdrawn NCT04687007 SMART-ALD - A New Lifestyle Intervention to Improve Quality of Life in Women With X-linked Adrenoleukodystrophy (X-ALD) No drug interventions supportive_care Not Available completed NCT04675749 Quality of Life in Women With X-linked Adrenoleukodystrophy No drug interventions Not Available Not Available recruiting NCT05911919 Validation of a Prognostic Biomarker Using Brain Diffusion MRI in X-linked Adrenoleukodystrophy No drug interventions Not Available Not Available not_yet_recruiting NCT01165060 The Effect of Bezafibrate on the Level of Very Long Chain Fatty Acids (VLCFA) in X-linked Adrenoleukodystrophy (X-ALD) treatment Not Available completed NCT02595489 A Pilot Study of Vitamin D in Boys With X-linked Adrenoleukodystrophy No drug interventions prevention 1 completed NCT03727555 Lentiviral Gene Therapy for X-ALD No drug interventions treatment Not Available unknown_status