Propionic Acidemia (PA) , Methylmalonic Acidemia (MMA) (DBCOND0126717)
Identifiers
- Synonyms
- Not Available
Associated Data
- Indicated Drugs and Targets
- Not Available
- Clinical Trials
Identifier Title Drug(s) Purpose Phase Status NCT04284917 Long-term Efficacy of Carglumic Acid in Organic Acidemia. treatment Not Available unknown_status