Propionic Acidemia (PA) , Methylmalonic Acidemia (MMA) (DBCOND0126717)

Identifiers

Synonyms
Not Available

Associated Data

Indicated Drugs and Targets
Not Available
Clinical Trials
IdentifierTitleDrug(s)PurposePhaseStatus
NCT04284917
Long-term Efficacy of Carglumic Acid in Organic Acidemia.treatmentNot Availableunknown_status