Hereditary Amyloidosis (DBCOND0159296)
Identifiers
- Synonyms
- Amyloidosis, Hereditary / Hereditary amyloidosis / Hereditary amyloidosis (disorder) / Familial amyloidosis / Amyloidosis, Familial / Neuropathic heredofamilial amyloidosis / Hereditary neuropathic amyloidosis / Amyloid Neuropathies, Familial / Familial amyloid polyneuropathy / Familial amyloid polyneuropathy (disorder)
Associated Data
- Indicated Drugs and Targets
- Not Available
- Clinical Trials
Identifier Title Drug(s) Purpose Phase Status NCT05940922 RWE-based Treatment Patterns and Outcomes in CIDP No drug interventions Not Available Not Available not_yet_recruiting NCT05879874 Prospective Evaluation of NfL as a Biomarker in ATTRv No drug interventions Not Available Not Available recruiting NCT05974644 Southeastern ATTR Amyloidosis Consortium: SEATTRAC Family Registry No drug interventions Not Available Not Available not_yet_recruiting NCT03759379 HELIOS-A: A Study of Vutrisiran (ALN-TTRSC02) in Patients With Hereditary Transthyretin Amyloidosis (hATTR Amyloidosis) treatment 3 active_not_recruiting NCT01960348 APOLLO: The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis treatment 3 completed NCT02939820 Expanded Access Protocol of Patisiran for Patients With Hereditary ATTR Amyloidosis (hATTR) Not Available Not Available approved_for_marketing NCT03400098 ATTR Expanded Access Program (EAP) by Ionis Not Available Not Available approved_for_marketing NCT02319005 ENDEAVOUR: Phase 3 Multicenter Study of Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) treatment 3 completed NCT05489549 Subclinical Transthyretin Cardiac Amyloidosis in V122I TTR Carriers No drug interventions Not Available Not Available recruiting NCT05873868 Myocardial Effects in Patients With ATTRv With Polyneuropathy Treated With Patisiran or Vutrisiran No drug interventions Not Available Not Available recruiting