Beta Thalassemia Transfusion Dependent
Also known as: Transfusion-dependent Beta-Thalassemia / Transfusion Dependent Beta-thalassemia / Transfusion Dependent Beta Thalassemia / Transfusion Dependent Beta-Thalassaemia
| Drug | Drug Name | Drug Description |
|---|---|---|
| DB15572 | Exagamglogene autotemcel | An autologous CRISPR-Cas9 modified hematopoietic stem cell therapy for the treatment of patients with sickle cell disease and recurrent vaso-occlusive crises. |
| Drug | Drug Name | Target | Type |
|---|
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB01609 | Deferasirox | 2 | Completed | 1 |
| DB16236 | Mitapivat | 3 | Active Not Recruiting | 1 |
| DB14546 | Sulfate ion | 3 | Active Not Recruiting | 1 |
| DB01041 | Thalidomide | 3 | Completed | 1 |